Ms Flaminia Macchia
Rare Diseases International
Executive Director
Prof. Dr. Milan Macek
Charles University Prague
Head of the Department of Biology and Medical Genetics - National Coordination Centre for Rare Diseases
Miss Divine Madhu
Cardiff University
Medical Student
Mrs Natalia Maeva
Bulgarian Society of the Patients with PH
President
Mrs. Natalia Maeva
Bulgarian society of patients with pulmonary hypertension
President
Ms Sylvie Maiella
Orphanet INSERM US14
International coordination manager
MR Abdelali Majdi
Ipsen Pharma SAS
VP Global Medical Affairs Rare Diseases
Dr Helen Malherbe
Rare Diseases South Africa NPC
Director of Research
Mrs. Cheena Malhotra
Crown Agents
Senior Health Specialist - Global Health
Miss Anaya Malik
EMJ
Editorial Manager
Ms Jelena Malinina
EURORDIS- Rare Diseases Europe
Patient Data Director
Mrs Maartje Mangelaars
Janssen
Patient Engagement Manager
Mrs Agnes Männik
EMA
Scientific Committee Manager
Mr Davide Marchi
Vertex Pharmaceuticals
Associate Director, International Patient Engagement
Mr Pietro Marinelli
Associazione SMITH-MAGENIS ASM17 ITALIA
President
Mrs Diana Marinello
ePAG
Volunteer, Network Manager
Mr. Lovro Markovic
Ministry of Health (AT)
Employee
Mrs Chahdil Maroua
INSERM
Developer
Dr Deborah Marsden
Ultragenyx
Global Medical Expert for Genetic Metabolic Disorders
Ms Jo Marshall
EURORDIS- Rare Diseases Europe
Corporate Relations Team