Ms Flaminia Macchia
Rare Diseases International
Executive Director

Prof. Dr. Milan Macek
Charles University Prague
Head of the Department of Biology and Medical Genetics - National Coordination Centre for Rare Diseases

Miss Divine Madhu
Cardiff University
Medical Student

Mrs Natalia Maeva
Bulgarian Society of the Patients with PH
President

Mrs. Natalia Maeva
Bulgarian society of patients with pulmonary hypertension
President

Ms Sylvie Maiella
Orphanet INSERM US14
International coordination manager

MR Abdelali Majdi
Ipsen Pharma SAS
VP Global Medical Affairs Rare Diseases

Dr Helen Malherbe
Rare Diseases South Africa NPC
Director of Research

Mrs. Cheena Malhotra
Crown Agents
Senior Health Specialist - Global Health

Miss Anaya Malik
EMJ
Editorial Manager

Ms Jelena Malinina
EURORDIS- Rare Diseases Europe
Patient Data Director

Mrs Maartje Mangelaars
Janssen
Patient Engagement Manager

Mrs Agnes Männik
EMA
Scientific Committee Manager

Mr Davide Marchi
Vertex Pharmaceuticals
Associate Director, International Patient Engagement

Mr Pietro Marinelli
Associazione SMITH-MAGENIS ASM17 ITALIA
President

Mrs Diana Marinello
ePAG
Volunteer, Network Manager

Mr. Lovro Markovic
Ministry of Health (AT)
Employee

Mrs Chahdil Maroua
INSERM
Developer

Dr Deborah Marsden
Ultragenyx
Global Medical Expert for Genetic Metabolic Disorders

Ms Jo Marshall
EURORDIS- Rare Diseases Europe
Corporate Relations Team